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Gene Therapy
Showing 11-20 of 29
Oleg A. Shchelochkov
Research TopicsDr. Shchelochkov's clinical research has focused on understanding the natural history of and novel therapeutic approaches to metabolic disor…
Kenneth A. Jacobson
Research TopicsResearch GoalOur overall goals are to design, chemically synthesize, and characterize pharmacologically new agonists and antagonists for the four…
John D. Heiss
Research TopicsDr. Heiss is actively involved in clinical and translational research to improve the treatment of degenerative brain diseases, brain tumors, canc…
John Chiorini
Research TopicsAdeno-associated virus (AAV) vectors have several characteristics that make them attractive agents for gene therapy, including stability, ease of…
Harry Lewis Malech
Research TopicsThe research program of GIS includes both clinical trials and basic bench research. Clinical trials include studies of gene therapy using ex vivo…
Frederick P. Dyda
Research Topicsp { margin-bottom: 0.1in; direction: ltr; line-height: 120%; text-align: left; widows: 0; orphans: 0 } a:link { so-language: zxx }The goal of our…
Cynthia "Cindy" Dunbar
Research TopicsOur research interests span basic laboratory studies through pioneering clinical trials focusing on stem cell biology and hematopoiesis—the devel…
Cynthia Tifft
Research TopicsImportant collaborations come from synergy between the clinic and the laboratory. This has been the hallmark of Dr. Tifft's research program…
Charles P. Venditti
Research TopicsThe research interests of the section surround the genetics, pathophysiology and treatment of the hereditary methylmalonic acidemias and disorder…