An official website of the United States government
Rare Diseases
Topics
- Anthrax
- Ataxia Telangiectasia
- Childhood Leukemia
- Congenital Muscular Dystrophy
- Cystic Fibrosis
- Esophageal Cancer
- Liver Cancer
- Malaria
- Mucopolysaccharidoses (MPS)
- Myasthenia Gravis
- Orphan Drugs
- Osteogenesis Imperfecta
- Pancreatic Cancer
- Spinal Muscular Atrophy
- Usher Syndrome
- Amyotrophic Lateral Sclerosis (ALS)
- Cooley's Anemia
- Hepatitis - A
- Muscular Dystrophy
- Pediatric Cardiomyopathy
- Primary Immunodeficiencies
- Transmissible Spongiform Encephalopathy (TSE)
- Tuberculosis
- Tuberculosis Vaccine
- Hodgkin's Disease
- Orthopox Viruses
- Paget's Disease
- Pediatric Cancer
- Spina Bifida
- Stomach Cancer
- Charcot-Marie-Tooth Disease
- Ovarian Cancer
- Sickle Cell Disease
- Dystonia
- Sudden Infant Death Syndrome
- Valley Fever
- Neuroblastoma
- West Nile Virus
- Neurofibromatosis
- Batten Disease
- Brain Cancer
- Vaginal Cancer
- Fragile X
- Huntington's Disease
- Hydrocephalus
- Rett Syndrome
- Tuberous Sclerosis